Takeda Presents $1 Million Gift to the Koch Institute for Integrative Cancer Research at MIT to Support Immuno-oncology Research

On February 8, 2017 Takeda Pharmaceutical Company Limited (TSE: 4502) and the Koch Institute for Integrative Cancer Research at MIT jointly reported that Takeda will support groundbreaking science in immuno-oncology at the Koch Institute (Press release, Takeda, FEB 8, 2017, View Source [SID1234517665]). Over the next two years, the $1 million gift will help to build upon the research currently being conducted by the Institute to investigate the role of the immune response in cancer and develop potential novel treatments.

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"Takeda embraces innovative science both inside and outside of our organization, and as part of our commitment to patients with cancer, we look to support academic institutions that are leading research in immuno-oncology," said Christopher Arendt, Ph.D., Immunology Discovery Lead at Takeda. "We are encouraged by the groundbreaking work underway at the Koch Institute in immuno-oncology, which has been a priority area of focus for Takeda and arguably one of the most significant breakthroughs in cancer research over the last few years. The Koch Institute’s dedication to the convergence of life sciences and engineering offers unique opportunities to advance this exciting field."

"The Koch Institute was created to promote the best in science and engineering to develop new approaches in the fight against cancer. Immuno-oncology is a major focus of our efforts, and we are grateful to Takeda for its support in this important area of research," said Tyler Jacks, Ph.D., Director, Koch Institute for Integrative Cancer Research.

Investigators at the Koch Institute are exploring the relationship between the immune system and cancer in animal models and human patients to improve immune responses to cancer. The Koch Institute works on the development of drug delivery tools, new methods for analyzing cellular immune responses and therapies based on engaging both the innate and the adaptive immune response, including therapeutic and preventative vaccines, as well as therapeutic antibodies through state-of-the art protein engineering methods.

OncoSec to Present New Clinical Data from Phase 2 Combination Study at ASCO-SITC Clinical Immuno-Oncology Symposium and Corporate Updates at Two Investment Conferences in February

On February 8, 2017 OncoSec Medical Incorporated ("OncoSec") (NASDAQ: ONCS), a company developing DNA-based intratumoral cancer immunotherapies, reported that it will present new clinical data on ImmunoPulse IL-12, its lead program focused on oncology, at the upcoming 2017 American Association for Cancer Research (AACR) (Free AACR Whitepaper) & Society for Immunotherapy of Cancer (SITC) (Free SITC Whitepaper) (ASCO-SITC) Clinical Immuno-Oncology Symposium. In addition, Punit Dhillon, President & CEO, will present a corporate overview at two investment conferences in February, including: the 19th Annual BIO CEO & Investor Conference and Source Capital Group’s 2017 Disruptive Growth & Healthcare Conference.

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2017 ASCO (Free ASCO Whitepaper)-SITC Clinical Immuno-Oncology Symposium
Dr. Alain Algazi, Associate Clinical Instructor, Department of Medicine (Hematology/Oncology), at the University of California San Francisco (UCSF) Helen Diller Family Comprehensive Cancer Center, will present an oral and poster presentation at the ASCO (Free ASCO Whitepaper)-SITC Clinical Immuno-Oncology Symposium to be held on February 23-24, 2017, in Orlando, FL.

Details of the presentation are as follows:

Abstract Title: Immune monitoring outcomes of patients with stage III/IV melanoma treated with a combination of pembrolizumab and intratumoral plasmid interleukin 12 (pIL-12) (Abstract ID #78)
Session Title: Activating the Immune System-New Clinical Approaches
Date and Time: February 23, 2017 at 11:30 a.m. – 1:00 p.m. (poster) & 3:30 p.m. – 5:00 p.m. EST (oral)
Location: Hyatt Regency Orlando

Further details on this ASCO (Free ASCO Whitepaper)-SITC oral and poster presentation will be provided in upcoming Company communications. For more information about this symposium, please visit: View Source

The 19th Annual BIO CEO & Investor Conference
Mr. Dhillon will present a corporate overview at The 19th Annual BIO CEO & Investor Conference on February 14 at 3:00 p.m. EST at The Waldorf Astoria in New York City.

To view to the live webcast, please access the following link at the time of the presentation: http://www.veracast.com/webcasts/bio/ceoinvestor2017/98226117037.cfm. An archived version of the webcast will be available for 90 days on OncoSec’s website: View Source

For more information about this conference, please visit: View Source

Source Capital Group’s 2017 Disruptive Growth & Healthcare Conference
Mr. Dhillon will present a corporate overview at Source Capital Group’s 2017 Disruptive Growth & Healthcare Conference on February 15 at 3:00 p.m. EST at Convene in New York City.

For more information about this conference, please visit: www.DisruptNYC.com.

MEI Pharma Reports Second Quarter Fiscal Year 2017 Results

On February 8, 2017 MEI Pharma, Inc. (Nasdaq: MEIP), an oncology company focused on the clinical development of novel therapies for cancer, reported results for its second quarter ended December 31, 2016 (Press release, MEI Pharma, FEB 8, 2017, View Source [SID1234517659]). The Company also highlighted recent clinical progress and outlined key milestones for the year ahead.

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"We begin the new calendar year with all of the pieces we need to be successful," said Daniel P. Gold, Ph.D., President and Chief Executive Officer of MEI Pharma. "We now have a partner with the operational and financial capabilities to support our Phase 3 AML program while we retain substantial long-term upside. We have a unique opportunity to return to MDS and apply what we learned in our prior studies with the prospect of significantly increasing the market potential for Pracinostat. We have two emerging drug candidates, ME-401 and ME-344, each expected to hit meaningful clinical inflection points in this year. And we have a healthy cash position to complement a strong clinical and regulatory team, all working to ensure that we execute on our development strategies. We’re poised for an exciting year ahead and I’m eager to share our progress as it unfolds."

Clinical Highlights

Prolonged survival evaluated in Phase 2 study of Pracinostat and azacitidine in AML. In December 2016, response and long-term survival data from a multi-center Phase 2 clinical study of the investigational drug candidate Pracinostat and azacitidine in elderly patients with acute myeloid leukemia (AML) who were not eligible for induction chemotherapy were presented at the American Society of Hematology (ASH) (Free ASH Whitepaper) Annual Meeting. Dr. Guillermo Garcia-Manero, MD Anderson Cancer Center, principal investigator of the study, reported a median overall survival of 19.1 (95%CI: 10.7-26.5) months, one-year survival of 62% and a complete response rate of 42%. The combination of Pracinostat and azacitidine was generally well tolerated, with no unexpected toxicities. The most common grade 3/4 treatment-emergent adverse events included febrile neutropenia, thrombocytopenia, anemia and fatigue. Pracinostat is an investigational agent and is not approved for use in the U.S.
Publication provides preliminary data for optimized dose of Pracinostat and azacitidine in MDS. In January 2017, results from a Phase 2, randomized, double-blind study of Pracinostat and azacitidine in patients with untreated, higher risk myelodysplastic syndromes (MDS) were published online ahead of print in the journal Cancer. The preliminary study data suggest that poor tolerability, which led to more frequent and earlier drug discontinuations in the Pracinostat group, likely limited the overall efficacy of the combination. However, in an analysis of patients who received at least 4 cycles of therapy, a tendency toward improved response duration and overall survival was observed in the Pracinostat group. The authors conclude that alternative dosing should be evaluated to determine the potential of the combination.
First patients dosed in Phase 1b study of PI3K delta inhibitor ME-401. In November 2016, a Phase 1b clinical study of ME-401 in patients with relapsed/refractory chronic lymphocytic leukemia (CLL) or follicular lymphoma began dosing patients. ME-401 is a potent and highly selective oral PI3K delta inhibitor with the potential for a wide therapeutic window that may lead to safer treatment options for patients with lymphomas. This study will enable the Company to study the safety and efficacy of ME-401 over time as it seeks to identify an optimal dose for Phase 2 studies.
Exposure data from Phase 1 study of ME-401 support improved therapeutic window. In November 2016, data from a first-in-human clinical study of ME-401 in healthy volunteers were presented at the American Association of Pharmaceutical Scientists Annual Meeting. The presentation highlighted the formulation selection and development of ME-401, including levels of drug exposure that support the potential for an improved therapeutic window compared to first-generation PI3K delta inhibitors.
First patients dosed in clinical study of mitochondrial inhibitor ME-344. In October 2016, an investigator-sponsored study of ME-344 in combination with the VEGF inhibitor bevacizumab (marketed as Avastin) in patients with recently diagnosed HER2-negative breast cancer began dosing patients. The randomized, placebo-controlled study is expected to enroll a total of 40 patients and is being conducted in collaboration with the Spanish National Cancer Research Centre in Madrid. Pre-clinical data from the collaboration showed substantially enhanced anti-tumor activity of ME-344 in cancer cells when combined with VEGF inhibitors due to a disruption of both mitochondrial and glycolytic metabolism.
Upcoming Milestones

Phase 3 study of Pracinostat in AML. In August 2016, the Company entered into an exclusive license, development and commercialization agreement with Helsinn Healthcare, SA (Helsinn License Agreement) for Pracinostat in AML and other potential indications. Under the terms of the Helsinn License Agreement, the Company will receive a $5 million milestone payment upon the earlier of (i) dosing of the first patient in a Phase 3 study of Pracinostat and azacitidine in newly diagnosed AML patients who are unfit to receive induction therapy or (ii) March 1, 2017.
Phase 2 study of Pracinostat in MDS. As part of the Helsinn License Agreement, the Company and Helsinn will work to explore an optimal dosing regimen of Pracinostat and azacitidine for the treatment of high and very high risk MDS. Enrollment in this study is anticipated to commence in the second quarter of calendar year 2017.
Phase 1b study of ME-401. This study of ME-401 in patients with relapsed/refractory CLL or follicular lymphoma is now actively dosing patients and interim data is expected in the second quarter of calendar year 2017.
Investigator-sponsored study of ME-344. This study of ME-344 and Avastin in patients with HER2-negative breast cancer is now actively dosing patients and interim data is expected in the second half of calendar year 2017.
Financial Highlights

As of December 31, 2016, the Company had $55.2 million in cash, cash equivalents and short-term investments, compared to $58.9 million as of September 30, 2016, with no outstanding debt. The Company believes its cash position will be sufficient to fund operations through at least fiscal year 2018.
Research and development expenses were $1.6 million for the three months ended December 31, 2016, and $3.3 million during the six months ended December 31, 2016. This compares with research and development expenses of $3.2 million for the three months ended December 31, 2015, and $6.0 million for the six months ended December 31, 2015. The decrease was primarily due to a reduction in clinical trial expenses for Pracinostat and ME-344.
General and administrative expenses were $2.0 million for the three months ended December 31, 2016, and $4.7 million for the six months ended December 31, 2016, compared to $1.9 million and $3.8 million, respectively, for the same periods in 2015. The year over year increase was primarily due to professional service costs associated with the Helsinn License Agreement.
Revenues were $17.2 million during the three months ended December 31, 2016, and $18.3 million during the six months ended December 31, 2016, related to the Helsinn License Agreement. During the three and six months ended December 31, 2016, the cost of research and development revenue was $1.8 million and $2.9 million respectively. Cost of research and development revenue is comprised primarily of reimbursable third-party pass-through costs.
Net income was $11.9 million, or $0.32 per basic and diluted share, for the three months ended December 31, 2016, and $7.6 million, or $0.21 per basic and diluted share, for the six months ended December 31, 2016. This compares to a net loss of $5.1 million, or $0.15 per basic and diluted share, for the quarter ended December 31, 2015, and a net loss of $9.7 million, or $0.28 per basic and diluted share for the six months ended December 31, 2015.

Five Prime to Present Preclinical Research Data at 2017 AACR Annual Meeting

On February 8, 2017 Five Prime Therapeutics, Inc. (Nasdaq:FPRX), a clinical-stage biotechnology company focused on discovering and developing innovative immuno-oncology protein therapeutics, reported that it will feature three new preclinical research poster presentations during the 2017 American Association for Cancer Research (AACR) (Free AACR Whitepaper) Annual Meeting, being held April 1 – 5, 2017, in Washington, D.C (Press release, Five Prime Therapeutics, FEB 8, 2017, View Source [SID1234517658]).

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Abstract Number and Title: #613, "Development of FPA154, a Novel Tetravalent Anti-GITR Antibody, for the Treatment of Solid Tumors"
Session Title: T-cell Immunity to Cancer: New Progress
Session Date and Time: Sunday, April 2, 2017, 1 – 5 p.m.
Location: Convention Center, Halls A-C, Poster Section 26, Poster Board Number: 17

Abstract Number and Title: #1599, "Antibody-Based Inhibition of CSF-1R as a Component of Combination Immunotherapy in Preclinical Models"
Session Title: Cytokines: The First Modern Immunotherapies
Session Date and Time: Monday, April 3, 2017, 8 a.m. – 12 p.m.
Location: Convention Center, Halls A-C, Poster Section 26, Poster Board Number: 7

Abstract Number and Title: #2633, "Identification of Novel T Cell Co-Inhibitory and Co-Stimulatory Receptors from Screening a Comprehensive Library of Extracellular Proteins"
Session Title: Checkpoints 2: Small-Molecule Inhibitors
Session Date and Time: Monday, April 3, 2017, 1- 5 p.m.
Location: Convention Center, Halls A-C, Poster Section 25, Poster Board Number: 22

Diffusion Pharmaceuticals’ TSC Phase 1/2 Glioblastoma Multiforme Clinical Trial Results Published in February 2017 Edition of Journal of Neurosurgery

On February 8, 2017 Feb. 08, 2017 (GLOBE NEWSWIRE) — Diffusion Pharmaceuticals Inc. (NASDAQ:DFFN), a clinical stage biotechnology company focused on the development of novel small molecule therapeutics for cancer and other hypoxia-related diseases, reported that the data from the Phase 1/2 clinical trial evaluating the safety and efficacy of trans sodium crocetinate (TSC) in newly diagnosed glioblastoma multiforme (GBM) has been published in the print edition of the peer-reviewed Journal of Neurosurgery ("JNS") (Volume 126, February 2017) (Press release, Diffusion Pharmaceuticals, FEB 8, 2017, View Source [SID1234517657]). Results from the Phase 1/2 clinical trial in 59 patients showed that 36.3% of the full TSC dose patients were alive at two years, compared to historical two-year survival rates ranging from 27% to 30%. TSC, the Company’s lead product candidate, is designed to target the tumor’s reduced oxygen microenvironment. TSC re-oxygenates cancerous tissue, thus making the cancer cells more susceptible to current radiation therapy and chemotherapy.

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"The publication of the article in the JNS provides peer-reviewed validation and raises the visibility of Diffusion across key stakeholder audiences," stated David Kalergis, Chairman and Chief Executive Officer. "The very encouraging data from our Phase 1/2 clinical trial supports our strategy to advance into Phase 3 clinical development."

The article, entitled, "Trans sodium crocetinate with temozolomide and radiation therapy for glioblastoma multiforme," outlines the results of a Phase 1/2 trial designed to evaluate the therapeutic effect of adding TSC to radiation therapy in 59 newly diagnosed GBM patients. In this trial, all patients received radiation with the drug temozolomide beginning either after surgery or biopsy of the tumor. TSC was administered around 45 minutes before each radiation session three days per week during the 6 weeks of radiation therapy. Considerable tumor shrinkage was seen in many patients, with tumors in 11 patients disappearing completely.

JNS is the official peer-reviewed publication of the American Association of Neurological Surgeons. Diffusion’s data was previously published in the online edition of JNS in May 2016 and was originally released in July 2015.

About Treatment-Resistant Cancers and TSC
Oxygen deprivation at the cellular level ("hypoxia") is the result of rapid tumor growth, causing the tumor to outgrow its blood supply. Cancerous tumor cells thrive with hypoxia and the resultant changes in the tumor microenvironment cause "treatment-resistance" to radiation therapy and chemotherapy. Using a novel, proprietary mechanism of action, Diffusion’s lead drug TSC counteracts tumor hypoxia – and therefore treatment-resistance – by safely re-oxygenating tumor tissue, thus enhancing tumor kill and potentially prolonging patients’ life expectancy. Oxygen levels of normal tissue remain unaffected upon administration of TSC, thereby avoiding the introduction of harmful side effects.