10-K – Annual report [Section 13 and 15(d), not S-K Item 405]

United Therapeutics has filed a 10-K – Annual report [Section 13 and 15(d), not S-K Item 405] with the U.S. Securities and Exchange Commission (Filing 10-K , United Therapeutics, FEB 24, 2015, View Source [SID1234501853]).

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10-K – Annual report [Section 13 and 15(d), not S-K Item 405]

Celldex Therapeutics has filed a 10-K – Annual report [Section 13 and 15(d), not S-K Item 405] with the U.S. Securities and Exchange Commission (Filing 10-K , Celldex Therapeutics, FEB 24, 2015, View Source [SID1234501842]).

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FORMA THERAPEUTICS ACHIEVES SECOND MAJOR OBJECTIVE IN COLLABORATION WITH CELGENE CORPORATION TO ADVANCE INNOVATIVE PROTEIN HOMEOSTASIS DRUGS

On February 24, 2015 FORMA Therapeutics reported that it has successfully met a second objective under its strategic collaboration agreement with Celgene, triggering an undisclosed payment from Celgene (Press release, Forma Therapeutics, FEB 24, 2015, View Source [SID:1234509332]). In April 2013, FORMA and Celgene entered into a collaboration to discover, develop and commercialize drug candidates to regulate protein homeostasis targets. This collaboration enables Celgene to evaluate selected targets and lead assets in protein homeostasis pathways during preclinical development.

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Steven Tregay, Ph.D., President and CEO, FORMA Therapeutics, said, "We are pleased to have identified novel chemical matter and robust chemical tool compounds which supported interrogation of the potential clinical utility for this target. Celgene’s steadfast commitment to oncology and novel areas of biology is testament to Celgene’s mission of improving the lives of patients worldwide. FORMA’s alliance with Celgene provides a unique opportunity to discover, advance and accelerate a broad pipeline of novel therapies to impact human health."

About Protein Homeostasis

Protein homeostasis, which is important in oncology, neurodegenerative and other disorders, involves a tightly regulated network of pathways controlling the biogenesis, folding, transport and degradation of proteins. Exploring the maintenance and regulation of such competing, yet integrated, biological pathways using a chemical biology approach should directly contribute to the understanding of diseases associated with excessive protein misfolding, aggregation and degradation.

PHASE III TRIAL OF ANTICANCER AGENT HALAVEN(R) IN SOFT TISSUE SARCOMA SHOWS OVERALL SURVIVAL BENEFIT IN PRIMARY ENDPOINT

On February 25, 2015 Eisai Co., reported that in a Phase III clinical trial (Study 309) of its in-house discovered and developed anticancer agent eribulin mesylate (“eribulin,” Brand name: Halaven) in patients with soft tissue sarcomas, eribulin demonstrated a statistically significant extension in overall survival (OS) over the comparator treatment dacarbazine, and the study met its primary endpoint (Press release Eisai, FEB 24, 2015, View Source [SID:1234501858]). No other systemic treatment for locally advanced or metastatic soft tissue sarcoma has been reported to extend overall survival in a Phase III study. Eribulin, as a single agent, has now demonstrated overall survival benefit in two distinct solid tumor types (metastatic breast cancer and soft tissue sarcomas), following two prior regimens in the advanced setting.

Study 309 was a randomized, open-label, multicenter, Phase III study comparing the efficacy and safety of eribulin versus dacarbazine in 452 patients (aged 18 or over) with locally advanced or recurrent and metastatic soft tissue sarcoma (one of two subtypes: adipocytic or leiomyosarcoma) who have disease progression following standard therapies which must have included an anthracycline and at least one other additional regimen. The primary endpoint of the study was to compare OS between both treatment arms. In this study, the most common adverse events observed in the eribulin arm were neutropenia, fatigue, nausea, alopecia, and constipation, which was consistent with the known side-effect profile of eribulin. Detailed results of the study will be presented at an academic conference in the near future.

Based on the results of Study 309, Eisai intends to submit applications during the first half fiscal 2015 to the regulatory authorities in multiple countries including Japan, the United States and Europe seeking an expansion of the indication for eribulin to include soft tissue sarcoma.

Soft tissue sarcoma is a rare form of malignant tumor with approximately 2,000 cases in Japan and approximately 12,000 cases in the United States diagnosed each year. In Europe, soft tissue sarcoma affects an estimated 4 to 5 out of every 100,000 people. While treatment of soft tissue sarcoma is focused on curative surgery, if the degree of malignancy is high,treatment then becomes a combination of chemotherapy and radiation therapy. As outcomes are poor for patients with advanced disease, it remains a disease with highly significant unmet medical needs. The study results have shown that eribulin has the potential to be an efficacious new treatment in this aggressive and complex cancer. Eribulin has been designated as an orphan drug for the treatment of soft tissue sarcoma in the United States and Japan.

First in the halichondrin class, Halaven is a microtubule dynamics inhibitor with a novel mechanism of action. It was first approved for the treatment of metastatic breast cancer in the United States in November 2010, and is currently approved in nearly 60 countries including Japan and countries in Europe, the Americas and Asia.

Eisai remains committed to providing further clinical evidence for eribulin aimed at maximizing value of the drug as it seeks to contribute further to addressing the diverse needs of, and increasing the benefits provided to, patients with cancer, their families, and healthcare providers.

Bavarian Nordic Announces Updated Overall Survival Data from Combination Immunotherapy Data of PROSTVAC plus Ipilimumab at the 2015 Genitourinary Cancers Symposium

On February 24, 2015 Bavarian Nordic reported that updated overall survival data from an NCI sponsored combination study of Bavarian Nordic’s active prostate cancer immunotherapy candidate PROSTVAC and ipilimumab, an immune checkpoint inhibitor will be presented at the Genitourinary Cancers Symposium in Orlando, FL on Thursday, February 26, 2015 (Press release Bavarian Nordic, FEB 24, 2015, View Source [SID:1234501841]).

30 patients with metastatic castration-resistant prostate cancer (mCRPC) were enrolled in the Phase 1 combination study. At the time of enrollment docetaxel was the only FDA-approved treatment that improved overall survival. The median predicted overall survival (OS) was 18.5 months. Patients were treated with PROSTVAC plus escalating doses of ipilimumab. The observed median OS was 31.3 months for all dose cohorts and 37.2 months for patients treated at 10 mg/kg based on updated overall survival data. Furthermore, approximately 20% of patients at 10 mg/kg remain alive at 80 months.

The senior author for the presentation as a poster is Dr. James L. Gulley, Laboratory of Tumor Immunology and Biology, National Cancer Institute at the National Institutes of Health. The presentation will take place during General Poster Session A on Thursday, February 26, 2015 from 11:30 AM – 1:00 PM EST at board H8. An abstract entitled: “Combining active immunotherapy and immune checkpoint inhibitors in prostate cancer” (Abstract #172) is also available online at View Source

Paul Chaplin, President & CEO of Bavarian Nordic, said: “The updated long-term survival data presented by our partners at NCI is further evidence of improved OS following treatment with PROSTVAC. These data represent perhaps the most compelling survival benefit seen to date in this late-stage setting, and provide a strong rationale to continue to evaluate the combination of PROSTVAC and checkpoint inhibitors in follow-on clinical studies. Given the unique product profile of PROSTVAC, with a favorable risk-benefit profile and ease of use, we see PROSTVAC as an ideal immunotherapy to combine with both approved and emerging therapies for prostate cancer and we look forward to exploring these further in the clinic.”