Data Presented at the Miami Breast Cancer Conference Show MammaPrint® and BluePrint® Accurately Predict Pathologic Complete Response Rate Regardless of Age

On March 4, 2021 Agendia, Inc., a world leader in precision oncology for breast cancer, reported new data from the prospective Neoadjuvant Breast Symphony Trial (NBRST) which demonstrate the predictive and prognostic abilities of MammaPrint and BluePrint, and underpin both assays’ pre-operative utility in pre-and post-menopausal patients (Press release, Agendia, MAR 4, 2021, View Source [SID1234576117]). A poster highlighting these findings will be presented at the 38th Annual Miami Breast Cancer Conference.

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The poster, entitled Pathologic Complete Response (pCR) Rates According to MammaPrint and BluePrint Results are Consistent Among Pre- and Post-Menopausal Patients, outlines the first age-based analyses of MammaPrint and BluePrint assays in the pre-operative setting. As expected, the data show that pCR rates varied according to molecular subtype, with MammaPrint and BluePrint accurately predicting pCR in patients of all subtypes, regardless of age. This analysis reinforces both tests’ use to better tailor pre-operative treatment and in determining the best timing for surgery for patients of all ages with breast cancer.

"Among the many clinically meaningful findings provided by the NBRST trial, we were focused on the importance of conducting a further sub-analysis of the trial’s data based on age," said William Audeh, MD, Chief Medical Officer of Agendia and a study author. "It is critical that we have a full understanding of the biology of each patient’s breast cancer, and whether age in itself affects the response to chemotherapy in the neoadjuvant setting. Our findings indicate that it is the genomic profile of the tumor, and not age of the patient, which determines response to chemotherapy. It is useful, in these challenging times, to know that we can triage each patient effectively with genomic tools that can give predictive and prognostic information essential for optimal treatment planning."

This age-based analysis reinforces the importance of the multi-disciplinary care team having meaningful genomic information at the earliest point after a diagnosis of breast cancer to inform the decision for the timing of surgery and systemic therapy. With recent analyses of pre-menopausal patients with breast cancer suggesting a clinical benefit to adjuvant chemotherapy, genomic tests that accurately predict outcomes across age ranges are crucial in the research community’s ongoing efforts to determine whether this age-dependent benefit is due to a direct cytotoxic effect on the tumor or a secondary hormonal effect due to ovarian suppression by chemotherapy.

"These data confirm that genomic tests, like MammaPrint and BluePrint, have a place in every breast cancer diagnosis," said James Pellicane, MD, Director of Breast Oncology at the Bon Secours Cancer Institute and an author of the poster. "Diving into the large bank of knowledge provided by the NBRST trial continues to help us facilitate more informed treatment decisions that will benefit the enormously diverse group of people who are diagnosed with breast cancer."

Agendia’s mission is to help guide the diagnosis and personalized treatment of breast cancer for all patients throughout their treatment journey, which the company prioritizes by continuing to look deeper into the arsenal of data that will help treat cancer.

Aldeyra Therapeutics Schedules Webcast and Conference Call to Report Full-Year 2020 Financial Results and Discuss Recent Business Highlights

On March 4, 2021 Aldeyra Therapeutics, Inc. (Nasdaq: ALDX) (Aldeyra) reported that it will host a conference call at 8:00 a.m. ET Thursday, March 11, 2021 to report financial results for the year ended December 31, 2020 and discuss recent business highlights (Press release, Aldeyra Therapeutics, MAR 4, 2021, View Source [SID1234576116]).

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The dial-in numbers are (866) 211-4098 for domestic callers and (647) 689-6613 for international callers. The Conference ID number is 6253616. A live webcast of the conference call will also be available on the Investors & Media page of the company’s corporate website at View Source

After the live webcast, the event will remain archived on the Aldeyra Therapeutics website for 90 days.

Syros Reports Fourth Quarter and Full Year 2020 Financial Results and Highlights Key Accomplishments and Upcoming Milestones

On March 4, 2021 Syros Pharmaceuticals (NASDAQ:SYRS), a leader in the development of medicines that control the expression of genes, reported financial results for the quarter and full year ended December 31, 2020, and provided an update on recent accomplishments and upcoming events (Press release, Syros Pharmaceuticals, MAR 4, 2021, View Source [SID1234576115]).

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"2021 promises to be a pivotal year for Syros," said Nancy Simonian, M.D., Chief Executive Officer of Syros. "We moved our lead program into our first registration-enabling study and continue to advance all three of our clinical-stage programs with the aim of setting new standards of care for targeted populations of patients with hematological malignancies and solid tumors. Following our recent financings, we are operating from a position of substantial strength, with capital to advance SY-1425, SY-2101 and SY-5609 through multiple expected data readouts while investing in our gene control platform to fuel our long-term pipeline. We are focused on executing with excellence as we accelerate toward our goal of bringing medicines to market that provide profound benefits for patients."

Upcoming Milestones

SY-1425: Oral RARα agonist

Initiate randomized Phase 2 trial of SY-1425 in combination with venetoclax and azacitidine in the second half of 2021 in RARA-positive newly diagnosed acute myeloid leukemia (AML) patients who are not suitable candidates for standard intensive chemotherapy.
Report initial data from the randomized Phase 2 trial in 2022.
SY-2101: Oral arsenic trioxide (ATO)

Initiate dose confirmation study of SY-2101 in the second half of 2021.
Report confirmatory dose and pharmacokinetic data in first half of 2022.
Initiate Phase 3 trial in 2022 in patients with newly diagnosed acute promyelocytic leukemia (APL).
SY-5609: Oral CDK7 inhibitor

Report additional dose-escalation data, including clinical activity data, in the third quarter of 2021 from the ongoing Phase 1 trial of SY-5609 in patients with breast, colorectal, lung, ovarian and pancreatic cancers, as well as in patients with solid tumors of any histology harboring Rb pathway alterations.
Initiate expansion portion of Phase 1 trial in the second half of 2021.
Gene control discovery engine

Nominate next development candidate in 2022.
Recent Pipeline Highlights

In February 2021, Syros opened its Phase 3 trial evaluating SY-1425 in combination with azacitidine in RARA-positive patients with newly diagnosed higher-risk myelodysplastic syndrome (HR-MDS) and is actively screening patients for enrollment. The double-blind, placebo-controlled trial is expected to enroll approximately 190 patients. Patients will be randomized 2:1 to receive SY-1425 in combination with azacitidine or placebo, respectively. The primary endpoint of the trial is complete response (CR) rate.
In December 2020, Syros presented new clinical data from its fully enrolled Phase 2 trial evaluating SY-1425 in combination with azacitidine in RARA-positive newly diagnosed unfit AML patients. The data, presented at the 62nd American Society of Hematology (ASH) (Free ASH Whitepaper) Annual Meeting, showed:
67% overall response rate, with a composite CR rate of 61%.
Median time to initial response of 1.2 months.
Median duration of response of 10.8 months, and median overall survival among patients who achieved a CR or CR with incomplete blood count recovery of 18 months.
The combination was generally well-tolerated, with no evidence of increased toxicity relative to either SY-1425 or azacitidine as a single agent.
Also at ASH (Free ASH Whitepaper), Syros presented new translational data demonstrating that most RARA-positive newly diagnosed unfit AML patients have a monocytic disease phenotype that is highly correlated with resistance to upfront treatment with venetoclax and azacitidine, suggesting that the RARA biomarker also selects for patients who are less likely to respond to treatment with venetoclax and azacitidine.
Recent Corporate Highlights

In January 2021, Syros completed an underwritten public offering of 5,400,000 shares of common stock, at a public offering price of $14.00 per share, resulting in gross proceeds of approximately $75.6 million, before underwriting discounts and commissions.
In December 2020, Syros acquired from Orsenix, LLC all of its assets related to SY-2101, a novel oral form of ATO. SY-2101 is a targeted clinical-stage drug candidate that has the potential to dramatically reduce the treatment burden of a standard-of-care regimen for newly diagnosed APL.
Also in December 2020, Syros announced the closing of a $90.5 million private financing with a group of institutional accredited investors. The financing was led by Bain Capital Life Sciences, with participation from new and existing investors, including Ally Bridge Group, Omega Funds, OrbiMed Advisors, EcoR1 Capital, and Samsara BioCapital.
Fourth Quarter and Full Year 2020 Financial Results

Revenues were $5.7 million for the fourth quarter of 2020, consisting of $3.6 million in revenue recognized under Syros’ collaboration with Global Blood Therapeutics, Inc. (GBT) and $2.1 million recognized under its collaboration with Incyte Corporation (Incyte). Revenues were $15.1 million for the year ended December 31, 2020, consisting of $11.7 million and $3.4 million from Syros’ collaborations with GBT and Incyte, respectively. Syros recognized $0.5 million and $2.0 million in revenue in the fourth quarter and full year 2019, respectively. All revenues recognized in 2019 were under Syros’ collaboration with Incyte.
Research and development expenses were $29.0 million for the fourth quarter of 2020 and $76.1 million for the year ended December 31, 2020, as compared to $14.3 million for the fourth quarter of 2019 and $58.2 million for the year ended December 31, 2019. This increase was primarily attributable to $12.0 million paid for the acquisition of SY-2101 from Orsenix, LLC and continued advancement of our clinical trials and preclinical programs.
General and administrative expenses were $5.9 million for the fourth quarter of 2020 and $21.3 million for the year ended December 31, 2020, as compared to $6.4 million for the fourth quarter of 2019 and $21.5 million for the year ended December 31, 2019.
For the fourth quarter of 2020, Syros reported a net loss of $30.1 million, or $0.62 per share, compared to a net loss of $19.7 million, or $0.46 per share, for the same period in 2019. For the full year ended December 31, 2020, Syros reported a net loss of $84.0 million, or $1.82 per share, compared to a net loss of $75.4 million, or $1.88 per share, for the same period in 2019.
Cash and Financial Guidance

Cash, cash equivalents and marketable securities as of December 31, 2020 were $174.0 million, as compared with $91.4 million on December 31, 2019. This increase reflects the $20 million upfront payment received in January 2020 in connection with Syros’ collaboration with GBT, $40.0 million in total that Syros drew from its senior secured loan facility with Oxford Finance, $12.3 million from the sale of common stock under Syros’ at-the-market sales facility in the first quarter of 2020 and the $90.5 million that Syros received from its December private placement, partially offset by the $12.0 million paid for the acquisition of SY-2101 from Orsenix, LLC and cash used to fund its operations. Cash, cash equivalents and marketable securities as of December 31, 2020 do not include gross proceeds of $75.6 million from the January 2021 public offering.

Based on its current plans, Syros believes that its existing cash, cash equivalents and marketable securities, including proceeds from its January 2021 public offering, will be sufficient to fund its planned operating expenses and capital expenditure requirements into 2023.

Conference Call and Webcast

Syros will host a conference call today at 8:30 a.m. ET to discuss these fourth quarter and full year 2020 financial results and provide a corporate update.

To access the live conference call, please dial 866-595-4538 (domestic) or 636-812-6496 (international), and refer to conference ID 4472467. A webcast of the call will also be available on the Investors & Media section of the Syros website at www.syros.com. An archived replay of the webcast will be available for approximately 30 days following the presentation.

Allarity Therapeutics Initiates Phase 2 Trial of IXEMPRA® in Europe for the Treatment of Metastatic Breast Cancer

On March 4, 2021 Allarity Therapeutics A/S ("Allarity" or the "Company") reported that it has enrolled the first patient in its European Phase 2 clinical trial of IXEMPRA (ixabepilone) for the treatment of metastatic breast cancer (Press release, Allarity Therapeutics, MAR 4, 2021, View Source [SID1234576114]).

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The U.S. Food and Drug Administration (FDA) approved IXEMPRA, a microtubulin inhibitor, in 2007 for the treatment of metastatic breast cancer. Allarity holds exclusive European option rights to IXEMPRA from the pharmaceutical company R-Pharm U.S., LLC, which previously acquired global rights to the drug from Bristol-Myers Squibb (BMS). Allarity has previously developed and validated a Drug Response Predictor (DRP) companion diagnostic specific for the drug.

"We are pleased to announce the enrollment of the first patient in our DRP-guided Phase 2 clinical trial for IXEMPRA, one of our prioritized pipeline programs. Phase 2 development of this asset in the European Union (EU) positions us to advance the drug toward a registrational approval and commercialization in this major oncology market, a necessary step for making it available to individuals living with metastatic breast cancer in Europe," commented Steve R. Carchedi, CEO of Allarity Therapeutics. "We are confident that our Phase 2 study will prove the merits of this drug, together with its DRP companion diagnostic, further clinically validating our DRP biomarker technology."

Allarity is currently conducting a DRP-guided Phase 2 clinical trial to evaluate IXEMPRA for the treatment of third-line metastatic breast cancer, with numerous trial sites planned in Europe, including Belgium, England, Denmark, Finland, Poland and Germany. The Company’s protocol plans for an enrollment target of 60 IXEMPRA DRP-selected patients. By using DRP for patient selection, Allarity aims to provide a superior clinical benefit to patients receiving IXEMPRA, as compared to historical clinical data from breast cancer patients treated with IXEMPRA but not selected with DRP. Principal Investigator Guy Jerusalem, M.D., Ph.D., Head of Medical Oncology and Director of the Breast Clinic at the University Hospital Center in Liege, Belgium, enrolled the first DRP-selected patient.

"I am pleased to see the first patient enrolled in our European Phase 2 trial for IXEMPRA," added Marie Foegh, M.D., D.Sc., CMO of Allarity Therapeutics. "We look forward to further evaluating the clinical and therapeutic value of our IXEMPRA DRP companion diagnostic, and to providing individuals with metastatic breast cancer another therapeutic option through our personalized medicine approach."

About the Drug Response Predictor – DRP Companion Diagnostic
Allarity uses its drug specific DRP to select those patients who, by the genetic signature of their cancer, are found to have a high likelihood of responding to the specific drug. By screening patients before treatment, the response rate can be significantly increased. The DRP method builds on the comparison of sensitive vs. resistant human cancer cell lines, including genomic information from cell lines combined with clinical tumor biology and prior clinical trial outcomes. DRP is based on messenger RNA from the patient’s biopsies. DRP has proven its ability to provide a statistically significant prediction of the clinical outcome from drug treatment in cancer patients in nearly 40 clinical studies that were examined, including an ongoing, prospective Phase 2 trial. The DRP platform can be used in all cancer types and is patented for more than 70 anti-cancer drugs.

Oncternal Therapeutics to Report Fourth Quarter 2020 Financial Results and Provide Business Update

On March 4, 2021 Oncternal Therapeutics, Inc. (Nasdaq: ONCT), a clinical-stage biopharmaceutical company focused on the development of novel oncology therapies, reported that it will report fourth quarter and full year 2020 financial results after the U.S. financial markets close on Thursday, March 11, 2021 (Press release, Oncternal Therapeutics, MAR 4, 2021, View Source [SID1234576113]). Oncternal’s management will host a webcast at 2:00 p.m. PT (5:00 p.m. ET) to discuss the Company’s financial results and provide a comprehensive business update.

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The live webcast of the call will be available online via a link from the investor relations page of the Company’s website at www.oncternal.com, and the call will be archived there for at least 30 days.