Bellicum to Participate in Two Upcoming Virtual Conferences

On September 28, 2020 Bellicum Pharmaceuticals, Inc. (NASDAQ:BLCM), a leader in developing novel, controllable cellular immunotherapies for cancers, reported that management will participate in two upcoming virtual conferences (Press release, Bellicum Pharmaceuticals, SEP 28, 2020, View Source [SID1234567679]).

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Conference Details:

Jefferies Cell Therapy Virtual Summit
Date/Time: Monday, October 5, 2020 at 11:30 a.m. EDT
Format: Fireside chat

2020 Virtual Cell & Gene Meeting on the Mesa
Date: Monday, October 12, 2020 – Friday, October 16, 2020
Format: Prerecorded company presentation will be available for registered attendees to view on-demand throughout the entirety of the conference. Please visit www.meetingonthemesa.com for full information including registration.

A live webcast of the fireside chat at the Jefferies Cell Therapy Summit may be accessed from the Events & Presentation section of the Bellicum website. An archived version of the Jefferies fireside chat will be available for replay following the event.

Sanofi completes Principia Biopharma Inc. acquisition

On September 28, 2020 Sanofi reported the successful completion of its acquisition of Principia Biopharma Inc. ("Principia") for $100 per share in cash (Press release, Sanofi, SEP 28, 2020, View Source [SID1234567678]).

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"The Principia acquisition further strengthens our core areas of autoimmune and allergic diseases, giving us full control of tolebrutinib (SAR442168), as well as additional BTK inhibitors to further develop," said Paul Hudson, Sanofi Chief Executive Officer. "The Principia integration into Sanofi augments our small molecule research capabilities as we look to maintain leadership in the discovery and development of oral medicines for serious illnesses."

The tender offer for all of the outstanding shares of Principia common stock expired as scheduled at one minute after 11:59 p.m., Eastern Time, on Friday, September 25, 2020. The minimum tender condition and all of the other conditions to the offer have been satisfied and on September 28, 2020, Sanofi and its wholly owned subsidiary Kortex Acquisition Corp. ("Purchaser"), accepted for payment and will promptly pay for all shares validly tendered and not validly withdrawn.

Following its acceptance of the tendered shares, Sanofi completed its acquisition of Principia through the merger of Purchaser with and into Principia, pursuant to Section 251(h) of the General Corporation Law of the State of Delaware, with Principia continuing as the surviving corporation and becoming an indirect, wholly owned subsidiary of Sanofi.

In connection with the merger, all Principia shares not validly tendered in the tender offer have been converted into the right to receive the same $100 per share in cash, without interest thereon and net of any applicable withholding taxes, that would have been paid had such shares been validly tendered in the tender offer. Principia common stock will cease to be traded on the NASDAQ Global Select Stock Market.

Evercore acted as financial advisor to Sanofi and Weil, Gotshal & Manges LLP acted as its legal counsel. Centerview Partners LLC and BofA Securities, Inc. acted as financial advisors to Principia and Cooley LLP acted as its legal counsel.

LabCorp to Announce Third Quarter Financial Results on October 27, 2020

On September 28, 2020 LabCorp (NYSE: LH) reported that it will release its third quarter of 2020 financial results before the market opens on Tuesday, Oct. 27, 2020, and then will host a conference call and webcast beginning at 9:00 a.m. EDT to discuss the results (Press release, LabCorp, SEP 28, 2020, View Source [SID1234567674]). The earnings release and accompanying financial information will be posted on the LabCorp Investor Relations website.

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Interested parties can access the conference call by dialing 1-877-898-8036 within the U.S. and Canada, or 1-720-634-2811 internationally, using the conference ID 4089862. In addition, a real-time webcast of the conference call will be available on the LabCorp Investor Relations website.

An audio replay of the conference call will be available from 1:00 p.m. EDT on Oct. 27, 2020, until 11:30 a.m. EDT on Nov. 10, 2020, by dialing 1-855-859-2056 within the U.S. and Canada, or 1-404-537-3406 internationally, using the conference ID 4089862. The webcast of the conference call will be archived and accessible through Oct. 13, 2021, on the LabCorp Investor Relations website.

UCLA researchers’ efforts to combat melanoma gets $13M boost from NIH

On September 28, 2020 UCLA researchers reported that have received a $13 million grant from the National Institutes of Health to find new ways to overcome melanoma resistance to some of the most promising targeted therapies and immunotherapies (Press release, University of California at Los Angeles, SEP 28, 2020, View Source [SID1234567673]).

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There have been significant advancements in the past decade using targeted therapies and immunotherapies for treating people with advanced forms of this deadliest type of skin cancer, but the treatments still only work in some people. Tumors can — and often do — become resistant to these drugs.

"While these therapies have transformed the way people with melanoma are treated, only about 40% to 50% of people respond to the therapies, and that is not good enough," said Dr. Antoni Ribas, one of the principal investigators on the grant, who is a professor of medicine at the David Geffen School of Medicine at UCLA and director of the Tumor Immunology Program at the UCLA Jonsson Comprehensive Cancer Center.

To further improve the response rate, identifying mechanisms that determine how tumors can become resistant to these therapies and understanding how to identify patients who will and will not respond to them is critical to developing new and improved treatments.

While melanoma is relatively rare — it accounts for only 1% of all skin cancer cases — rates of melanoma have been rising rapidly over the past few decades, and it is responsible for the vast majority of skin cancer deaths, according to the American Cancer Society. An estimated 100,000 new cases of melanoma will be diagnosed in the U.S. in 2020, and nearly 7,000 Americans will die from the disease this year.

The five-year grant will allow researchers to investigate the biology of these therapies and will also fund clinical trials to develop new combination therapies to defeat melanoma resistance.

Along with Ribas, Dr. Roger Lo, a professor of medicine and director of the melanoma clinic in the UCLA Division of Dermatology, and Thomas Graeber, a professor of molecular and medical pharmacology and director of the UCLA Metabolomics Center, are leading the effort.

"These funded projects will allow us to take earlier findings and move them into pre-clinical models and clinical trials to advance treatments for tumors that do not respond or become resistant to current therapies," said Graeber.

The interdisciplinary research team, whose members have been collaborating for over a decade, will be focusing on three translational research projects:

Understanding the resistance of NRAS-mutated melanomas: Lo is investigating ways to block multiple resistance routes in melanomas with the NRAS gene mutation and to combine and sequence targeted therapies and immunotherapies. By characterizing and co-targeting genomic, epigenomic, proteomic and immunologic alterations that resist therapies, the team will be able to reveal the landscape of resistance.

Targeting ferroptosis to block the de-differentiation resistance escape route: One way cancers escape targeted treatments is to de-differentiate, or change the type of cell they are into an earlier stage of development. This change of identity allows the cells to be less dependent on the pathway that was otherwise being effectively targeted. Graeber is investigating cell subtypes that de-differentiate and have shown sensitivity to a type of self-inflicted cell death called ferroptosis, which can potentially block melanoma cells attempting to take this escape route. Using ferroptosis-inducing drugs in combination with current standard treatments could potentially strengthen the response rate.

Studying resistance mechanisms in PD-1 blockade immunotherapy: This project, led by Ribas, is looking at how interferon-gamma, an immune response–stimulating signaling molecule that helps activate immune cells, guides the treatment response in people with advanced melanoma who are treated with one of the leading immunotherapies, called PD-1 blockade. Understanding how interferon-gamma genes work can potentially be used to predict a response to immunotherapy and for rationalizing new combination treatments that induce interferon signaling that can be used to treat more patients.

"All of our research addresses problems that require integrated and collaborative work with one another," Lo said. "Sharing resources has been instrumental in moving our work forward, and this grant will help us move faster in the lab, enabling us to create therapies for more people who desperately need it."

Ribas, Lo and Graeber are all members of the UCLA Jonsson Comprehensive Cancer Center and the Eli and Edythe Broad Center of Regenerative Medicine and Stem Cell Research at UCLA.

Palatin Technologies, Inc. Announces Fourth Quarter and Fiscal Year 2020 Financial Results and Provides a Business Update

On September 28, 2020 Palatin Technologies, Inc. (NYSE American: PTN), a specialized biopharmaceutical company developing first-in-class medicines based on molecules that modulate the activity of the melanocortin and natriuretic peptide receptor systems, reported financial results for its fourth quarter and fiscal year ended June 30, 2020 (Press release, Palatin Technologies, SEP 28, 2020, View Source [SID1234567672]).

Fourth Quarter and Fiscal Year 2020 Financial Highlights

●Net loss for the fourth quarter ended June 30, 2020 was $(7.3) million, or $(0.03) per basic and diluted share, compared to net income of $52.2 million, or $0.25 per basic and $0.23 per diluted share for the comparable quarter of 2019;
●Net loss for the year ended June 30, 2020 was $(22.4) million, or $(0.10) per basic and diluted share, compared to net income of $35.8 million, or $0.17 per basic and $0.16 per diluted share for the year ended June 30, 2019;
●The difference between the quarter and year ended June 30, 2020 compared to the quarter and year ended June 30, 2019 was due to the recognition of license and contract revenue pursuant to our license agreement with AMAG of $60.3 million for the quarter and year ended June 30, 2019;
●As of June 30, 2020, the Company had $82.9 million in cash and cash equivalents, compared to $43.5 million as of June 30, 2019, and no debt.

Recent Business Highlights and Updates

●In July 2020 mutually terminated the January 2017 license agreement granting AMAG Pharmaceuticals ("AMAG") exclusive North American rights to market Vyleesi (bremelanotide), the first and only on demand treatment for premenopausal women suffering from acquired, generalized, hypoactive sexual desire disorder (HSDD), a condition affecting one in ten premenopausal women;
●Completed enrollment of a Phase 2 clinical study with PL9643 for the treatment of dry eye disease (DED). Final patient and topline data readout is targeted for the fourth calendar quarter of 2020;
●A Phase 2 proof-of-concept clinical study with an oral formulation of PL8177 in ulcerative colitis patients is targeted to start in the first half of calendar year 2021.

"We are pleased to have completed enrollment last month in our PL9643 Phase 2 clinical study in subjects with dry eye disease. Data readout is targeted for the fourth calendar quarter of 2020. We believe that, if approved, PL9643’s potentially quick onset to efficacy and favorable tolerability and safety profile may provide a treatment option to the millions of individuals suffering from DED," stated Carl Spana, Ph.D., President and CEO of Palatin.

"We believe that Vyleesi is an important treatment for the millions of premenopausal women suffering from HSDD. Our goal with the Vyleesi program is to demonstrate value in the marketplace by increasing patient demand and access. Our objective is to re-license the U.S. rights to a committed women’s healthcare company. Having taken steps to ensure no disruption for patient access to Vyleesi, we are working to expand awareness of the condition and treatment in a highly-targeted and informed manner, enhance and stream-line patient access, and increase insurance coverage."

Dr. Spana further commented, "Our strong cash position of $83 million at June 30, 2020 and no debt, coupled with the $12 million received in July 2020 from AMAG, plus an additional $4.3 million due from AMAG March 31, 2021, provides us the financial resources to significantly advance our Anti-Inflammatory and Autoimmune programs, and make complimentary targeted investments to our Vyleesi program."

"The entire Palatin team thanks healthcare workers across the nation for their selfless efforts in the treatment and care of COVID-19 patients. I would also like to thank all of our employees for their dedication and commitment to ensure the advancement of our development programs and clinical trial patient support," continued Spana. "Although Palatin has experienced limited adverse impact on operations from the pandemic, we are cognizant there may be further disruptions to business activity based on a resurgence of the virus and have taken steps to be as prepared as possible for this potential outcome."

Programs Overview

Hypoactive Sexual Desire Disorder (HSDD) / Vyleesi (bremelanotide injection)

In July 2020, Palatin announced the mutual termination of its License Agreement with AMAG for Vyleesi. Under the terms of the termination agreement, Palatin regained all North American development and commercialization rights for Vyleesi. AMAG made a $12.0 million payment to Palatin at closing and will make a $4.3 million payment to Palatin on March 31, 2021. Palatin assumed all Vyleesi manufacturing agreements, and AMAG will transfer all information, data, and assets related exclusively to Vyleesi, including, but not limited to, existing inventory. AMAG will provide certain transitional services to Palatin for a period of time to ensure continued patient access to Vyleesi and regulatory compliance during the transition back to Palatin. Palatin will reimburse AMAG for the agreed upon costs of the transition services.

Palatin is exploring its options pertaining to enhancing the commercialization of Vyleesi, including but not limited to, discussions with potential collaboration partners that currently market female healthcare products. Palatin continues collaboration discussions for territories outside the currently licensed territories of China and Korea and anticipates executing multiple agreements through calendar year 2021.

In the interim, the Company’s strategy implements an informed and highly targeted approach to marketing, focusing on telemedicine, social media, and digital advertising. The Company is committed to working with payers and healthcare professionals to ensure women with HSDD have continued and affordable access to Vyleesi. Vyleesi remains commercially available through specialty pharmacies Avella and BioPlus. Patients also have the ability to connect with a healthcare provider through telemedicine. Patients and healthcare providers can learn more about HSDD and Vyleesi at www.vyleesi.com.

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Vyleesi is the first FDA-approved product for the as-needed treatment for premenopausal women who experience distress or interpersonal difficulty due to low sexual desire. This treatment is available as a subcutaneous self-injection in a prefilled disposable autoinjector pen for use in anticipation of a sexual encounter.

Anti-Inflammatory / Autoimmune Programs

Enrollment in a Phase 2 clinical study with PL9643 was completed in August 2020. Data readout is targeted for the fourth calendar quarter of 2020. If results from the Phase 2 study support advancing to Phase 3, the Company will initiate a Phase 3 efficacy study as early as mid-calendar year 2021.

A Phase 2 proof-of-concept clinical study with an oral formulation of PL8177 in ulcerative colitis patients is targeted to start in the first half of calendar year 2021, with data readout potentially in the first half of calendar year 2022.

The Company continues its assessment and development work related to the treatment of patients with diabetic retinopathy, with an IND targeted for mid-calendar year 2021.

The Company currently anticipates filing an IND and commencing clinical trials with PL8177 for non-infectious uveitis, for which FDA granted orphan drug designation, in the second half of calendar year 2021.

Palatin is advancing its COVID-19 development plan and is conducting all the required activities needed to file an IND and begin clinical studies with PL8177 in COVID-19 patients. These activities will be completed in the fourth calendar quarter of 2020, allowing the Company to potentially file an IND with the FDA and initiate a clinical study of PL8177 for the treatment of COVID-19 patients early in the first calendar quarter of 2021.

The landscape for treating and conducting clinical studies in COVID-19 patients is rapidly evolving. This impacts the design, risk, and ability to conduct clinical studies in COVID-19 patients. Considering the risk and uncertainty of conducting COVID-19 clinical studies, the start of a PL8177 clinical study is subject to receiving external funding and operational support. The Company is in the process of applying to government programs that provide such support.

Natriuretic Peptide Receptor (NPR) System Program

PL3994, an NPR-A agonist, will be evaluated in a Phase 2A clinical study in heart failure patients with preserved ejection fraction. The proposed study is a collaboration with two major academic medical centers and is supported by an American Heart Association grant. The study is now anticipated to start patient enrollment in the fourth calendar quarter of 2020

Genetic Obesity Program

Palatin’s melanocortin receptor 4 (MC4r) peptide PL8905 and orally active small molecule PL9610 are currently under investigation for the treatment of rare genetic metabolic and obesity disorders. These programs are under internal evaluation for orphan designations, potential development, and licensing.

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Fourth Quarter and Fiscal Year 2020 Financial Results

Revenue

Palatin recognized no revenues for the quarter ended June 30, 2020 and $117,989 in license and contract revenue for the year ended June 30, 2020 related to our license agreement with AMAG.

For the quarter and year ended June 30, 2019, Palatin recognized $60.3 million in license and contract revenue related to our license agreement with AMAG.

Operating Expenses

Total operating expenses for the quarter ended June 30, 2020 were $7.4 million compared to $8.1 million for the comparable quarter of 2019. The decrease in operating expenses was due to the overall reduction in research and development expenses and a decrease in general and administrative expenses.

For the year ended June 30, 2020, Palatin incurred $23.7 million of operating expenses, compared to $24.6 million for the year ended June 30, 2019. The decrease in operating expenses was due to the overall reduction in research and development expenses offset by an increase in general and administrative expenses.

Other Income/Expense, net

Total other income, net, for the quarter and year ended June 30, 2020 was $90,667 and $1.2 million, respectively.

Total other income, net, for the quarter and year ended June 30, 2019 was $38,476 and $28,707, respectively.

The difference is related primarily to the increase in investment income and secondarily to the decrease in interest expense related to venture debt.

Cash Position

Palatin’s cash and cash equivalents were $82.9 million with no accounts receivable as of June 30, 2020, compared to cash and cash equivalents of $43.5 with accounts receivable of $60.3 million at June 30, 2019.

Management believes that its existing capital resources will be sufficient to fund the Company’s planned operations through at least September 30, 2021.

Conference Call / Webcast

Palatin will host a conference call and audio webcast on September 28, 2020 at 11:00 a.m. Eastern Time to discuss the results of operations in greater detail and provide an update on corporate developments. Individuals interested in listening to the conference call live can dial 1-800-353-6461 (US/Canada) or 1-334-323-0501 (international), conference ID 6978729. The audio webcast and replay can be accessed by logging on to the "Investor/Webcasts" section of Palatin’s website at View Source A telephone and audio webcast replay will be available approximately one hour after the completion of the call. To access the telephone replay, dial 1-888-203-1112 (US/Canada) or 1-719-457-0820 (international), passcode 6978729. The webcast and telephone replay will be available through October 5, 2020.

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