New positive interim data in Phase 2 study
of SNT-5505 in myelofibrosis

On June 13, 2025 Syntara Limited (ASX:SNT), a clinical-stage drug development company, reported further positive interim data from its ongoing Phase 2 clinical trial evaluating SNT-5505 (200 mg BID) in combination with ruxolitinib (RUX) for the treatment of myelofibrosis (MF) (Press release, Syntara, JUN 13, 2025, View Source;v=04711220c3a57065317ba4efca4a3459a4e46882 [SID1234653852]). This data will be presented at the European Hematology Association (EHA) (Free EHA Whitepaper) Conference on Sunday 15 June 2025 AEST, and builds upon the positive interim results announced at the American Society of Hematology (ASH) (Free ASH Whitepaper) Annual Meeting in December 2024.

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The latest interim results further highlight the safety and clinical benefits of SNT5505’s unique mechanism of action and competitive profile in treating MF patients who have had a suboptimal response to existing standard of care.

Patients in the trial had been treated with ruxolitinib (RUX) for an average of three years with symptom scores, spleen sizes and blood counts indicative of high disease burden.

Highlights:

73% (8/11) of evaluable patients achieved TSS50 at 24 weeks of treatment or beyond.

44% (4/9) of evaluable patients achieved a spleen volume reduction (SVR) of 25% at Week 24 or beyond. Notably there were no increases in dosage of concomitant RUX that might otherwise explain the impact of SNT-5505 on spleen volume.

The continued improvement in patient symptoms and spleen volume is a novel finding that differentiates SNT-5505 from MF drugs on market and in later stages of development. It highlights the potential of SNT-5505 to be used in combination with JAK inhibitors to change the long-term outcomes for MF patients.

SNT-5505 is safe and well tolerated, with no treatment related serious adverse events (SAEs) attributed to SNT-5505; providing additional and important differentiation to MF drugs on market and in development.

Syntara to engage with the FDA in Q3 on study results and trial design for a pivotal Phase 2c/3 study.

Syntara CEO Gary Phillips commented: "After very recently being awarded Fast Track designation, the positive interim data to be presented at EHA (Free EHA Whitepaper) 2025 further reinforces the promising profile of SNT5505 as an add-on therapy for myelofibrosis patients with a suboptimal response to existing standard of care. The sustained and increasing improvements in both symptom burden and spleen volume, coupled with its excellent safety and tolerability, continue to differentiate SNT-5505 from other drugs in this space. We are particularly encouraged by the durability of the responses observed and look forward to reporting final study results and engaging with the FDA and potential partners in the coming months."

Alligator Bioscience receives FDA endorsement of mitazalimab Phase 3 dose for pancreatic cancer

On June 13, 2025 Alligator Bioscience (Nasdaq Stockholm: ATORX), a clinical-stage biotechnology company developing tumor-directed immunotherapies, reported that the U.S. Food and Drug Administration (FDA) has provided feedback supporting the selection of the 900 µg/kg dose of its CD40 agonist mitazalimab for the planned Phase 3 study in metastatic pancreatic ductal adenocarcinoma (mPDAC) (Press release, Alligator Bioscience, JUN 13, 2025, View Source [SID1234653851]).

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This positive regulatory feedback confirms Alligator’s dose selection and represents a key milestone in the late-stage development of mitazalimab.

"We are very pleased with the FDA’s timely and constructive response. This marks an important step forward as we finalize our Phase 3 program for mitazalimab in one of the most aggressive and underserved cancers. We are now in active partnering dialogues aiming to secure the right partner to take mitazalimab into Phase 3," said Søren Bregenholt, CEO of Alligator Bioscience.

SABRE topline results: Cu-64 SAR-Bombesin is effective in detecting prostate cancer recurrence in patients with negative SOC imaging

On June 13, 2025 Clarity Pharmaceuticals (ASX: CU6) ("Clarity" or "Company"), a clinical-stage radiopharmaceutical company with a mission to develop next-generation products that improve treatment outcomes for patients with cancer, reported positive topline results from the diagnostic Phase II SABRE trial (NCT05407311)1 with 64Cu-SAR-Bombesin in participants with PSMA-negative BCR of prostate cancer following definitive therapy (Press release, Clarity Pharmaceuticals, JUN 13, 2025, View Source [SID1234653843]). SAR-Bombesin targets the GRPR present on cells of a range of cancers, including prostate cancer.

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SABRE trial design
SABRE (Copper-64 SAR-Bombesin in Biochemical Recurrence of prostate cancer) was a Phase II multi-centre, single arm, non-randomised, open-label copper-64 labelled SAR-Bombesin PET imaging trial of patients with PSMA-negative BCR of prostate cancer following definitive therapy. To be considered for inclusion in the study, candidates were required to demonstrate negative or equivocal findings for prostate cancer on approved PSMA PET (68Ga-PSMA-11 or 18F-DCFPyL), anatomical imaging (CT and/or magnetic resonance imaging [MRI]) and any other SOC imaging, if available. The primary objectives of the trial were to investigate the safety and tolerability of the product as well as its ability to correctly detect recurrence of prostate cancer.

Study participants were dosed with 200 MBq of 64Cu-SAR-Bombesin and underwent PET/CT scans at 1-4 hours and 24 ± 6 hours post-dose (same-day and next-day imaging, respectively). The scans were interpreted by three blinded central readers. To determine the efficacy of 64Cu-SAR-Bombesin imaging, the same-day and next-day PET/CT results of the central readers were assessed against a composite reference standard that was determined by an independent, blinded, central expert panel. The reference standard consisted of histopathology, follow-up SOC imaging and/or confirmed prostate-specific antigen (PSA) response to focal therapy.

The primary efficacy endpoints were participant-level CDR (defined as the proportion of true-positive participants out of all scanned participants who had at least one evaluable reference standard datapoint collected) and region-level PPV (defined as the proportion of true-positive regions out of all positive regions on the 64Cu-SAR-Bombesin PET/CT scan with corresponding evaluable composite reference standard data), assessed independently for same-day and next-day imaging timepoints.

The design of the SABRE study followed advice from regulators to achieve the highest standards in clinical research in the BCR setting. Based on this guidance, the expert panel, who determined the reference standard, was blinded to the results of the 64Cu-SAR-Bombesin scans and distinct from the central readers assessing the 64Cu-SAR-Bombesin scans. This approach removed potential biases in the assessment of the reference standard, which was not the case for other studies conducted in this setting.

The SABRE study design also adopted a conservative approach to the analysis of both co-primary endpoints. If a lesion identified on the 64Cu-SAR-Bombesin scan was not biopsied, and it was also not present on follow-up SOC imaging (a suboptimal reference standard with known low sensitivity and in a patient population that was negative on SOC imaging at screening), it was considered as false-positive in the analysis by default.

Topline results
Fifty-three patients with negative or equivocal SOC scans at screening (which included approved PSMA PET and anatomical imaging) were enrolled and imaged. Forty-seven participants were evaluable for the primary efficacy endpoints. Approximately half of the participants enrolled had PSA less than or equal to 1.0 ng/mL at study entry.

The average detection rate across readers using 64Cu-SAR-Bombesin PET/CT was 35.2% on same-day imaging (24.5%-43.4% range) and 27.7% on next-day imaging (17%-37.7% range). Approximately 47 lesions were identified on same-day imaging (40-59 range) and approximately 52 on next-day imaging (24-95 range), despite these patients having negative or equivocal SOC scans prior to study entry, highlighting the potential clinical benefit that imaging with 64Cu-SAR-Bombesin can provide. The most common site of lesion detection was in the lymph nodes (LNs) and the prostate regions.

The participant-level CDR was 14.9% (95% CI: 6.2, 28.3) on same-day imaging and ranged from 4.3% to 14.9% (95% CI: 0.5-28.3) on next-day imaging across the readers. Region-level PPV ranged from 22.6% to 47.1% (95% CI: 9.6-72.2) on same-day imaging and from 22.2% to 37.5% (95% CI: 2.8-61.7) on next-day imaging.

The CDR and PPV results were substantially impacted by the large number of lesions that were detected on the 64Cu-SAR-Bombesin scans, but unable to be verified due to the lack of effective diagnostic options available for comparison and biopsy not being clinically appropriate in most cases. Three patients underwent biopsy (the ‘gold standard’ for verifying lesions) due to the findings of the 64Cu-SAR-Bombesin scan and a total of four biopsies were performed. All biopsies were positive for prostate cancer, including two pelvic LNs, one extra-pelvic LN and one bone lesion.

Administration of 64Cu-SAR-Bombesin at 200 MBq was shown to be safe and well tolerated. Only two participants had AEs related to 64Cu-SAR-Bombesin with all being mild (Grade 1) and resolving within 2 days of onset.

Case study
A participant with BCR of prostate cancer presented with a baseline PSA of 22.3 ng/mL, negative SOC PSMA PET (18F-DCFPyL, Figure 1, left image) and equivocal CT at screening. Imaging with 64Cu-SAR-Bombesin (middle image) revealed substantial disease burden with lesions detected in the pelvic LNs, extra-pelvic LNs, visceral/soft tissue, and bone. Subsequent biopsies of a right pelvic bone lesion and a supradiaphragmatic LN confirmed malignancy at both sites. A follow-up 18F-DCFPyL PET scan, conducted approximately 4 months after the screening with 18F-DCFPyL, failed to detect lesions in all regions except for the bone.

Clarity’s Executive Chairperson, Dr Alan Taylor, commented, "The SABRE trial represents an important milestone for Clarity, setting a new benchmark by seeking to identify lesions that do not express PSMA. This trial, which is Clarity’s first sponsored study with 64Cu-SAR-Bombesin, has now shown that this product can provide a solution where the current diagnostic options fall short and improve lesion detection beyond what is achievable with SOC PSMA-targeted imaging. Prostate cancer is characterised by significant biological heterogeneity, where some patients, or even individual lesions within the same patient, may lack PSMA expression and remain undetectable on PSMA-targeted imaging. A PET agent targeting an alternative receptor, such as GRPR, which is expressed in up to 100% of prostate cancers2-6, may allow for better staging and hence more accurate treatment of BCR prostate cancer. As seen in the SABRE trial, some patients have widespread metastatic disease that remains completely undetectable by all available SOC imaging for extended periods. These patients deserve access to advanced diagnostic tools, such as 64Cu-SAR-Bombesin PET, that can reveal otherwise hidden disease and open the door to more informed and effective treatment options.

"We are very pleased with these results of the SABRE trial as a first look into this extraordinary patient population that has virtually invisible disease using SOC imaging and therefore, by definition, a very high unmet medical need. The data confirms that 64Cu-SAR-Bombesin is safe, well tolerated, and effective at detecting prostate cancer recurrence. Up to approximately 43% of participants had a positive 64Cu-SAR-Bombesin PET/CT, demonstrating the potential scale of the diagnostic gap this novel agent may help address with no disease identified by SOC imaging. These results are also corroborated by the findings of an earlier investigator-initiated trial (IIT), BOP, conducted by Prof Louise Emmett at St Vincents Hospital Sydney, where 64Cu-SAR-Bombesin PET/CT identified disease recurrence in 44% of participants with BCR of prostate cancer and negative or equivocal 68Ga-PSMA-11 PET/CT7.

"The lack of any suitable diagnostic options for these men is made clear by the difficulty faced in validating lesions detected by 64Cu-SAR-Bombesin. Given we identified a large number of lesions with our product, it was not feasible nor ethical to verify all lesions with biopsy. Verification of the findings by other means, such as SOC imaging, was further complicated by the very nature of the trial, which specifically enrolled patients who were negative or equivocal on all available SOC imaging. These inherent challenges led to a high number of lesions not being confirmed as true-positives in the study. However, the fact that prostate cancer was confirmed in all 64Cu-SAR-Bombesin PET-positive lesions that were biopsied strongly reinforces the potential clinical value of this agent and the need it may fulfill within the current diagnostic landscape. SABRE has provided valuable insights into the performance of 64Cu-SAR-Bombesin relative to available SOC imaging. The study findings, including the potential for significantly improved lesion detection, will be carefully considered in the design of a registrational trial.

"We now have three exceptional diagnostic agents in various stages of clinical development, 64Cu-SAR-bisPSMA, 64Cu-SARTATE and 64Cu-SAR-Bombesin, and all three are showing impressive efficacy compared to SOC imaging. We look forward to sharing additional data readouts from all trials and progressing discussions with key medical experts to determine the most effective pathway for registration, particularly with this asset, 64Cu-SAR-Bombesin, as the pathway to commercialisation for 64Cu-SAR-bisPSMA and 64Cu-SARTATE is clearly defined and quickly progressing. We have already explored additional indications expressing GRPR with high unmet needs where 64Cu-SAR-Bombesin may significantly improve the diagnostic landscape, and we have seen some promising data on the benefits of 64Cu-SAR-Bombesin PET/CT in breast cancer patients from the C-BOBCAT IIT, also conducted by Professor Louise Emmett. Results from this study showed high lesion uptake of 64Cu-SAR-Bombesin in women with lobular subtype of metastatic breast cancer in comparison to SOC imaging (i.e. CT, bone scan and 18F-FDG PET/CT), indicating that our imaging agent could offer improved diagnostic options in this indication8.

"These encouraging findings from the SABRE, BOP and C-BOBCAT trials, as well as other trials with GRPR-targeted agents in other cancers, highlight the broad potential of 64Cu-SAR-Bombesin to become a best-in-class diagnostic agent in a number of indications. This reinforces our drive to advance Targeted Copper Theranostics in areas of significant clinical need, as these areas lack not only accurate diagnostics, but also effective therapeutics. The detection of GRPR-expressing cancers could represent a significant opportunity to enable more comprehensive disease assessment across varied tumour phenotypes. We look forward to working with key regulatory groups, such as the US Food and Drug Administration (FDA), to explore various avenues and indications with SAR-Bombesin further as we continually strive to improve diagnostic and theranostic options for patients and their clinicians."

About SAR-Bomesin
64Cu-SAR-Bombesin is a highly targeted pan-cancer radiopharmaceutical with broad cancer application. It targets the GRPR present on cells of a range of cancers, including but not limited to prostate, breast and ovarian cancers. GRPR is found in up to 100% of prostate cancers, including prostate cancers that don’t express PSMA (PSMA-negative)2-6. The product utilises Clarity’s proprietary sarcophagine (SAR) technology that securely holds copper isotopes inside a cage-like structure, called a chelator. Unlike other commercially available chelators, the SAR technology prevents copper leakage into the body. SAR-Bombesin is a Targeted Copper Theranostic (TCT) that can be used with isotopes of copper-64 (Cu-64 or 64Cu) for imaging and copper-67 (Cu-67 or 67Cu) for therapy.

About Prostate Cancer
Prostate cancer is the second most common cancer diagnosed in men globally and the fifth leading cause of cancer death in men worldwide9. The American Cancer Institute estimates in 2025 there will be about 313,780 new cases of prostate cancer in the US and around 35,770 deaths from the disease10.

Approximately 20-25% of prostate cancer patients with BCR have low or no uptake of PSMA-targeting tracer11-14. These patients are unlikely to show meaningful uptake of PSMA-targeted products, such as 68Ga-PSMA-11. Given the prostate cancer indication is one of the largest in oncology, there is a significant unmet medical need in this segment.

BBOT Announces Publication in Science Highlighting Preclinical Data that Supports the Potential for RAS:PI3Kα Breaker BBO-10203 to Provide Therapeutic Benefit across Multiple Tumor Types

On June 12, 2025 TheRas, Inc. d/b/a BBOT (the "Company"), a clinical-stage biopharmaceutical company focused on RAS-pathway malignancies, reported the publication of preclinical data supporting the potential for BBO-10203 to provide therapeutic benefit across multiple tumor types (Press release, BridgeBio Oncology Therapeutics, JUN 12, 2025, View Source [SID1234653871]). The publication, titled "BBO-10203 inhibits tumor growth without inducing hyperglycemia by blocking RAS-PI3Kα interaction" was published in the peer-reviewed journal Science.

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These data describe the discovery and preclinical evaluation of BBO-10203, a first-in-class, orally available inhibitor that selectively blocks the interaction between RAS proteins and PI3Kα without impairing insulin signaling. By covalently binding to a unique cysteine in the RAS-binding domain of PI3Kα, BBO-10203 effectively disrupts oncogenic RAS-driven activation of the PI3Kα pathway across a range of tumor types, including those with mutations in KRAS, PIK3CA, and HER2 amplification, without inducing hyperglycemia. The compound showed broad antitumor activity in vitro and in vivo and demonstrated enhanced efficacy when combined with targeted therapies such as CDK4/6 inhibitors, ER antagonists, HER2 inhibitors, and KRASG12C inhibitors. These findings support the potential of BBO-10203 as a well-tolerated, mechanistically distinct therapeutic for PI3Kα- and RAS-driven cancers.

"Because the contribution of the second most mutated signaling pathway in human cancers remains underappreciated, we searched for an entirely novel molecular mechanism that is not encumbered by known metabolic liabilities to inhibit PI3Kα signaling," said Pedro Beltran, PhD, Chief Scientific Officer of BBOT. "By blocking the crosstalk between RAS and PI3Kα in tumors, without interfering with physiological insulin signaling, we believe BBO-10203 represents a fundamentally differentiated approach with both biological and therapeutic promise."

"This work stemmed from our goal to elucidate the structural basis of RAS:PI3Kα binding and therapeutically target this interaction," said Dhirendra Simanshu, PhD, lead author and Principal Scientist at Frederick National Laboratory for Cancer Research (FNLCR). "Our findings show that targeting RAS-effector interactions is both structurally tractable and has potential across a range of cancers. BBO-10203 exemplifies a paradigm shift – rather than inhibiting RAS directly, it intercepts oncogenic signaling through effectors like PI3Kα, enabling tumor suppression while preserving essential physiological functions."

BBO-10203 is currently being evaluated in our Phase 1 BREAKER-101 study (NCT06625775) in patients with locally advanced or metastatic HER2+ breast cancer, HR+/HER2- breast cancer, KRAS mutant advanced CRC, and KRAS mutant advanced NSCLC. The discovery of BBO-10203 was the result of a collaboration between the RAS Initiative at Frederick National Laboratory, Lawrence Livermore National Laboratory, and BBOT.

"This work is an excellent example of chemistry bringing clarity to biology," said Frank McCormick, PhD, FRS, Chairman of the BBOT Board, Advisor to the National Cancer Institute’s RAS Initiative at Frederick National Laboratory for Cancer Research, and Professor of Tumor Biology and Cancer Research at UCSF. "The role of the RAS:PI3Kα interaction in cancer biology has long been suspected but challenging to pin down precisely. Now we understand which cancers depend on this interaction, some quite unexpected. With BBO-10203 now in the clinic, there’s real hope that these discoveries will translate into meaningful benefit for many cancer patients."

Samsung Bioepis Presents Long-Term Safety Data of EPYSQLI™ (Eculizumab) in PNH at the European Hematology Association (EHA) Congress 2025

On June 12, 2025 Samsung Bioepis Co., Ltd. ("Samsung Bioepis") reported the long-term safety data of EPYSQLI (eculizumab; SB12), a biosimilar to Soliris1, in paroxysmal nocturnal hemoglobinuria (PNH) at the European Hematology Association (EHA) (Free EHA Whitepaper) Congress 2025 held at Milan, Italy from June 12 to 15 (Press release, Samsung Bioepis, JUN 12, 2025, View Source [SID1234653870]).

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EPYSQLI was approved by the European Commission (EC) for the treatment of paroxysmal nocturnal hemoglobinuria (PNH) and atypical hemolytic uremic syndrome (aHUS) in May 2023 and March 2024, respectively2.

The study assessed the long-term safety of EPYSQLI in PNH patients by evaluating the consistency of safety outcomes, particularly serious adverse events (SAEs) between the initial 52-week Phase 3 study period and the extended treatment (ET) period, spanning from 52 weeks to up to 158 weeks. The same maintenance dose of 900 mg EPYSQLI was administered every 2 weeks. A total of 46 patients from the Phase 3 study received ET. During ET, seven patients (15.2%) experienced a total of 14 SAEs with no occurrence of fatal cases, and all patients fully recovered without permanently discontinuing the treatment. The exposure-adjusted event rate (EAER) was comparable between initial 52-week period and ET period (EAER were 0.13 and 0.17, respectively), and there was no statistically difference between initial 52-week and ET period in EAER (p-value = 0.76). The study is consistent with the findings of the Phase 3 study with no newly identified safety signals and no fatal cases occurred throughout the entire treatment period with all SAEs resolving completely.

Details of the abstract are as follows3:

Abstract title: Long-Term Safety of SB12 in Paroxysmal Nocturnal Hemoglobinuria: Up to 2-year Extension Treatment Safety Data
Abstract number: PB2811
Type: Publication Only
Session title: Bone marrow failure syndromes incl. PNH – Clinical
Author(s): Jun Ho Jang, Siook Baek, Yumin Baek, Jinah Jung, Ciprian Tomuleasa, Hanna Oliynyk, Theerin Lanamtieng, Soo Min Lim
Besides approval by the EC, EPYSQLI is also approved by the U.S. Food and Drug Administration (FDA) and Korea’s Ministry of Food and Drug Safety (MFDS) as a biosimilar to Soliris. In countries where EPYSQLI is approved and available, EPYSQLI may not be prescribed and/or dispensed for its unapproved other indications for which Soliris is approved.

About EPYSQLI (Eculizumab Biosimilar) in the European Union (EU)
EPYSQLI is indicated in adults and children for the treatment of paroxysmal nocturnal hemoglobinuria (PNH) and atypical hemolytic uremic syndrome (aHUS). EPYSQLI is not approved for and should not be used for the treatment of generalised myasthenia gravis (gMG) and neuromyelitis optica spectrum disorder (NMOSD). EPYSQLI must be administered by a healthcare professional and under the supervision of a physician experienced in the management of patients with hematological disorders or renal disorders.

EPYSQLI EU Important Safety Information
The EU Summary of Product Characteristics for EPYSQLI includes the following Special warning and Precautions:

Meningococcal Infection
Due to its mechanism of action, the use of eculizumab increases the patient’s susceptibility to meningococcal infection (Neisseria meningitidis). Meningococcal disease due to any serogroup may occur. To reduce the risk of infection, all patients must be vaccinated at least 2 weeks prior to receiving eculizumab unless the risk of delaying eculizumab therapy outweighs the risks of developing a meningococcal infection. Patients who initiate eculizumab treatment less than 2 weeks after receiving a tetravalent meningococcal vaccine must receive treatment with appropriate prophylactic antibiotics until 2 weeks after vaccination. Vaccines against serogroups A, C, Y, W 135 are recommended in preventing the commonly pathogenic meningococcal serogroups. Vaccine against serogroup B where available is also recommended. Patients must receive vaccination according to current national vaccination guidelines for vaccination use.

Vaccination may further activate complement. As a result, patients with complement-mediated diseases, including PNH and aHUS, may experience increased signs and symptoms of their underlying disease, such as haemolysis (PNH) or TMA (aHUS). Therefore, patients should be closely monitored for disease symptoms after recommended vaccination.

Vaccination may not be sufficient to prevent meningococcal infection. Consideration should be given to official guidance on the appropriate use of antibacterial agents. Cases of serious or fatal meningococcal infections have been reported in eculizumab-treated patients. Sepsis is a common presentation of meningococcal infections in patients treated with eculizumab. All patients should be monitored for early signs of meningococcal infection, evaluated immediately if infection is suspected, and treated with appropriate antibiotics if necessary. Patients should be informed of these signs and symptoms and steps taken to seek medical care immediately.

Other Systemic Infections
Patients may have increased susceptibility to other type of serious infections, especially with Neisseria and encapsulated bacteria.

Infusion Reactions
Administration of eculizumab may result in infusion reactions or immunogenicity that could cause allergic or hypersensitivity reactions (including anaphylaxis). Eculizumab administration should be interrupted in all patients experiencing severe infusion reactions and appropriate medical therapy administered.

Anticoagulant therapy
Treatment with eculizumab should not alter anticoagulant management.

PNH Laboratory Monitoring
PNH patients should be monitored for signs and symptoms of intravascular haemolysis, including serum lactate dehydrogenase (LDH) levels, and may require dose adjustment within the recommended 14±2 day dosing schedule during the maintenance phase (up to every 12 days).

aHUS Laboratory Monitoring
aHUS patients receiving eculizumab therapy should be monitored for thrombotic microangiopathy by measuring platelet counts, serum LDH and serum creatinine, and may require dose adjustment within the recommended 14±2 day dosing schedule during the maintenance phase (up to every 12 days).

Treatment Discontinuation for PNH
If patients discontinue treatment with eculizumab they should be closely monitored for signs and symptoms of serious intravascular haemolysis.

Treatment Discontinuation for aHUS
If aHUS patients discontinue treatment with eculizumab, they should be monitored closely for signs and symptoms of severe thrombotic microangiopathy complications.

The most common adverse reaction observed with eculizumab treatment in clinical trials was headache, (occurred mostly in the initial phase of dosing), and the most serious adverse reaction was found to be meningococcal infection.

Refer to the Summary of Product Characteristics for EPYSQLI’s full safety information.